Exonics Therapeutics, Cambridge, MA

Exonics Therapeutics

www.exonicstx.com

Exonics Therapeutics was launched in February 2017 to advance the research of our scientific founder, Dr. Eric Olson and his laboratory at the University of Texas Southwestern Medical Center (UTSW) to develop treatments for patients with neuromuscular diseases. Dr. Olson is one of the world’s leading experts in the study of muscle cells and the application of gene editing to treat these types of diseases. In particular, Dr. Olson’s laboratory has used adeno-associated virus (AAV) to deliver a CRISPR/Cas9 technology that can identify and repair exon mutations to restore the production of dystrophin, a protein that helps stabilize and protect ...

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Number of Employees: 0-25
Annual Revenue: $0-1 Million

www.exonicstx.com
One Broadway 14th Floor
Cambridge, MA USA 02142

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