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Abeona Therapeutics is focused on developing and delivering gene therapy and plasma-based products for severe and life-threatening rare diseases. Abeona’s lead program is an adeno-associated virus (AAV)-based gene therapy for Sanfilippo syndrome (MPS IIIA and IIIB) in collaboration with patient advocate groups, researchers and clinicians. Clinical trials for Sanfilippo types A and B are anticipated to begin in 2015.
The Ohio State University Medical Center (OSUMC) is a multidisciplinary academic medical center located in Columbus, Ohio
Emerging leader in prescription digital therapeutics
ONYX Healthcare USA is a Brea, CA-based company in the Healthcare, Pharmaceuticals, and Biotech sector.